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wiedeman_steiner_syndrome [2026/05/26 14:23] – created Scott Larsonwiedeman_steiner_syndrome [2026/05/26 14:46] (current) – [Resources] Scott Larson
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 ======Wiedemann-Steiner Syndrome ====== ======Wiedemann-Steiner Syndrome ======
-FIXME 
  
 ====Main Features==== ====Main Features====
-  *  +  * Developmental delay/Intellectual disability 
 +  * Hypotonia 
 +  * Distinctive Facial Features 
  
 ====Eye Findings==== ====Eye Findings====
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   * Microphthalmia (rare)    * Microphthalmia (rare) 
 ====Other Findings==== ====Other Findings====
-  * +  * Failure to thrive 
 +  * Short stature 
 +  * Constipation  
 +  * Heart defects 
 +    * PDA, ASD 
 +  * GU 
 +    * renal calyceal dilation, uterine anomalies 
 +  * Immune 
 +    * Hypogammaglobulinemia and  recurrent infections 
 +  * Endocrine  
 +    * Growth Hormone deficiency 
 +    * Hypothyroidism 
 +    * premature thelarche 
 +  * Skeletal 
 +    * Vertebral anomalies  
 +    * accelerated skeletal maturation, hypdysplasia brachydactyly, clinodactyly 
 +  * CNS 
 +    * Seizures  
 +    * polymicrogyria, hypoplasia of corpus callosum, Chiari malformation, tethered cord  
 ====Etiology==== ====Etiology====
-  * +  * Heterozygous (monoallelic) pathologic variant of the KMT2A gene located on chromosome 11q23.  
 +    * KMT2A regulates gene expression during development  
 +  * Prevalence is about 1:25,000 to 40,000.  
 ====Resources==== ====Resources====
   * [[https://www.ncbi.nlm.nih.gov/books/NBK580718/|Gene Reviews Summary]]   * [[https://www.ncbi.nlm.nih.gov/books/NBK580718/|Gene Reviews Summary]]
-  * [[https://onlinelibrary.wiley.com/doi/10.1111/cge.12586| +  * [[https://onlinelibrary.wiley.com/doi/10.1111/cge.12586| Delineation of clinical features in Wiedemann–Steiner syndrome caused by KMT2A mutations. Miyake N. et al. Clinical Genetics 2015;89(1):115-119]]
  
 {{tag>syndrome}} {{tag>syndrome}}